Posted by Michael Wonder on 20 Jul 2018
ICER releases draft evidence report on inotersen and patisiran for hereditary transthyretin amyloidosis
20 July 2018 - Public comment period now open until 17 August; requests to make oral comment during public meeting also being accepted.
The ICER today released a draft evidence report assessing the comparative clinical effectiveness of inotersen (Akcea Therapeutics) and patisiran (Alnylam Pharmaceuticals) for hereditary transthyretin-related amyloidosis, a rare genetic condition that can affect that can affect multiple organ systems.
The report, along with accompanying draft voting questions, will be open to public comment until 17 August 2018. Findings contained in this report are preliminary and subject to change based on additional stakeholder input and further analysis of data. The report will be subject to deliberation during a public meeting of the Midwest Comparative Effectiveness Public Advisory Council (Midwest CEPAC), one of ICER’s three independent evidence appraisal committees, in September of 2018.
