FDA approves first therapy for rare disease that causes low phosphate blood levels, bone softening

FDA

18 June 2020 - Today, the U.S. Food and Drug Administration approved Crysvita (burosumab-twza) injection to treat patients age two and older with tumour-induced osteomalacia, a rare disease that is characterised by the development of tumours that cause weakened and softened bones. 

The tumours associated with tumour-induced osteomalacia release a peptide hormone-like substance known as fibroblast growth factor 23 that lowers phosphate levels.

Read FDA press release

Michael Wonder

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Michael Wonder

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Outcome , Medicine , US , Paediatrics